Scientists are testing an entirely new way to fight heart disease: whether gene editing might offer a one-time fix for high ...

The idea of self-amplifying gene editing is to get cells to pass on packages of CRISPR machinery to their neighbours, boosting the effect ...

Faced with a life-threatening metabolic disease, KJ’s doctors at Children’s Hospital of Philadelphia sprinted to create a ...

For most of his 20 years, a New Jersey man knew pain as a daily reality. Now, after a one-time CRISPR gene-editing treatment at Children's Hospital of Philadelphia, Austin Louis says he is finally ...

A research team has successfully demonstrated the world's first gene-editing treatment for Leber's hereditary optic ...

Explore groundbreaking gene-editing therapy for kidney disease, offering hope to those with polycystic kidney disease.

In this webinar, researchers discuss using and improving next-generation gene editing approaches for targeted, accurate, and ...

Researchers developed a topical gene therapy that corrects disease-causing mutations in human skin models using lipid nanoparticles and gene editing. The approach restored skin function and could be ...

A new skin-applied gene therapy uses lipid nanoparticles to deliver gene editing into skin stem cells, correcting ...

VIPs gathered last week for the final beam placement in Children’s Hospital of Philadelphia’s new 26-story tower. But the ...