Regenxbio's Duchenne gene therapy shows improved muscle function in trial

March 11 (Reuters) - Regenxbio said on Wednesday that interim data from a early-to-mid stage study of its experimental gene therapy in patients with Duchenne muscular dystrophy showed continued ...
KSDK

'You won't be alone': Families unite at Forest Park for MDA Muscle Walk

ST. LOUIS — On a cloudy morning in Forest Park, families gathered not just to take steps together but to take them for each other. The Muscular Dystrophy Association's 2025 Muscle Walk on May 4 drew ...

Save Our Sons Foundation leads 92km Perth walk to raise money for kids with Duchenne muscular dystrophy

Families affected by the condition and a dedicated support crew walked 92km across Perth over four days to raise funds and ...

First successes in the development of a gene therapy for incurable LAMA2-related muscular dystrophy

Researchers at the University of Basel have developed a gene therapy that could potentially treat a rare and currently fatal muscle disease in children. The study shows in animal models that a single ...
Forbes

The Triumphs And Trials Of Duchenne Gene Therapy

Forbes contributors publish independent expert analyses and insights. William A. Haseltine, Ph.D., covers genomics and regenerative medicine Today, the world stands at a crossroads in genetic medicine ...