Nine-year follow-up of gene therapy in haemophilia B confirms long-term safety and reduced bleeding, though full capsid ...

Delivery of therapeutic genes is essential for gene therapy. Adeno-associated viruses (AAVs) are a prime vector for carrying ...

Validated, tissue-specific library enables customisable and controllable liver-targeted gene expression with high specificity and minimal off-target activity in muscle tissue ...

D Molecular Therapeutics™, 4DMT™, Therapeutic Vector Evolution™, and the 4DMT logo are trademarks of 4DMT. All of the Company’s product candidates are in clinical or preclinical development and have ...

As Super Bowl 50 turns ten, the halftime collaboration between Coldplay, Beyoncé, and Bruno Mars feels more historically ...

This proteomics-driven approach to drug discovery improves target validation and uncovers insights into undruggable proteins, ...

After facing a delayed decision deadline and a clinical hold, Regenxbio’s Hunter syndrome gene therapy has been rejected by ...

Yeast-based protein expression systems will likely play an important role in vaccine production during future pandemics.

There’s a Chinese expression—zuò shan guan hǔ dòu—which roughly translates to “Sit on the mountain and watch tigers fight.” ...

We have all seen it. The shuffle of sketches as an illustrator spreads them out for eager eyes, the tiny puff of breath as a ...

New AAV therapy for retinitis pigmentosa completes Phase I/II dosing, aiming to protect cones and slow vision loss; first ...

Guggenheim Securities Emerging Outlook: Biotech Summit 2026 February 12, 2026 12:30 PM ESTCompany ParticipantsR.